Table 1 Population

Infused patients

11

 Crigler-Najjar

6

  Type 1

5

  Type 2

1

 Urea cycle defect

5

  OTC deficiency

4

  Arginase deficiency

1

 Female

7

 Male

4

Age at infusion

0.9–16.25 year(s)

 12.5 × 10⁶/kg

4

 50 × 10⁶/kg

2

 200 × 10⁶/kg

5

Total number of infusions

1–10

Total number of days of infusions

1–4

Completed infusion cycles

7